UNLOCK THE POTENTIAL BENEFITS OF SPINRAZA
SPINRAZA has been studied in the largest clinical trial program conducted to date in spinal muscular atrophy (SMA)
SPINRAZA was evaluated in a broad range of SMA types
SPINRAZA has been shown in clinical trials to change the expected course of SMA for some individuals, increasing survival, motor milestone achievement, and motor function.
The effectiveness of SPINRAZA was established in the pivotal ENDEAR and CHERISH clinical trials and supported by additional trials across a broad range of SMA types and levels of function.
What are controlled and open-label studies?
Clinical studies are designed to determine whether a medication is effective and to monitor for any side effects. In a controlled study, there are treated and untreated groups, and the researchers and patients do not know who is receiving the drug. In an open-label study, both researchers and patients know what treatment is being given.